Calbi, Valeria
Fumagalli, Francesca
Consiglieri, Giulia
Penati, Rachele
Acquati, Serena
Redaelli, Daniela
Attanasio, Vanessa
Marcella, Facchini
Cicalese, Maria Pia
Migliavacca, Maddalena
Barzaghi, Federica
Ferrua, Francesca
Assanelli, Andrea
Silvani, Paolo
Zoccolillo, Matteo
Chidini, Giovanna
Chiesa, Robert
Arora, Ruchi
Ciotti, Francesca
Sarzana, Marina
Antonioli, Gigliola
Baldoli, Cristina
Morena, Francesco
Martino, Sabata
Ardissino, Gian Luigi
Sora, Maria Grazia Natali
Naldini, Luigi
Ciceri, Fabio
Aiuti, Alessandro
Bernardo, Maria Ester
Article History
Received: 4 November 2017
Revised: 7 December 2017
Accepted: 16 December 2017
First Online: 29 January 2018
Compliance with ethical standards
:
: Fondazione Telethon and Ospedale San Raffaele developed gene therapy for MLD which was licensed by GSK AA is Principal Investigator of the TIGET-MLD gene therapy trial. FF is the Principal Investigator of the MLD natural history study. The remaining authors declare that they have no conflict of interest.