Doccini, Stefano
Morani, Federica
Nesti, Claudia
Pezzini, Francesco http://orcid.org/0000-0003-1590-4558
Calza, Giulio
Soliymani, Rabah
Signore, Giovanni
Rocchiccioli, Silvia
Kanninen, Katja M.
Huuskonen, Mikko T.
Baumann, Marc H.
Simonati, Alessandro
Lalowski, Maciej M. http://orcid.org/0000-0002-3683-4096
Santorelli, Filippo M. http://orcid.org/0000-0002-1359-9062
Article History
Received: 3 February 2020
Revised: 27 February 2020
Accepted: 4 March 2020
First Online: 30 March 2020
Conflict of interest
: Alessandro Simonati received honoraria for consultancy from Bio-Marin Pharmaceutical, Inc and Neurogene Co; the remaining authors declare that they have no conflict of interest.