Rich, Kelly A. http://orcid.org/0000-0002-0027-0313
Wier, Christopher G.
Russo, Jessica
Kong, Lingling
Heilman, Patrick L.
Reynolds, Anthony
Knapp, Amy
Pino, Megan G.
Keckley, Elizabeth
Mattox, Lori
Malbrue, Raphael A.
Sumner, Charlotte J. http://orcid.org/0000-0001-5088-6012
Buhimschi, Catalin
Kolb, Stephen J. http://orcid.org/0000-0002-8503-8459
Funding for this research was provided by:
Spinal Muscular Atrophy Foundation
CJS has served as a paid advisor, consultant, and/or speaker to the SMA Foundation, Biogen, Ionis Pharmaceuticals, PTC Therapeutics, Roche/Genentech, Sarepta, NuraBio, AveXis, and Novartis.
Article History
Received: 28 April 2021
Revised: 27 October 2021
Accepted: 5 November 2021
First Online: 22 November 2021
Competing interests
: SJK has received compensation for consultation from AveXis, Biogen, and Genentech. CJS receives grant support from Roche Ltd and has served as a paid advisor, consultant, and/or speaker to the SMA Foundation, Biogen, Ionis Pharmaceuticals, PTC Therapeutics, Roche/Genentech, Sarepta, NuraBio, AveXis, and Novartis. All other authors report no competing interests.