Kazi, Zoheb B.
Desai, Ankit K.
Troxler, R. Bradley
Kronn, David
Packman, Seymour
Sabbadini, Marta
Rizzo, William B.
Scherer, Katalin
Abdul-Rahman, Omar
Tanpaiboon, Pranoot
Nampoothiri, Sheela
Gupta, Neerja
Feigenbaum, Annette
Niyazov, Dmitriy M.
Sherry, Langston
Segel, Reeval
McVie-Wylie, Alison
Sung, Crystal
Joseph, Alexandra M.
Richards, Susan
Kishnani, Priya S.
Article History
Received: 11 April 2018
Accepted: 3 August 2018
First Online: 14 September 2018
Disclosure
: Z.B.K. received grant support from the Lysosomal Disease Network; Sanofi Genzyme. A.K.D. received grant support from Sanofi Genzyme. D.K. received research funding from Sanofi Genzyme and New York Medical College. S.P. is a recipient of a research grant from Sanofi Genzyme, member of Sanofi Genzyme speakers’ bureau, and participant in a clinical trial of an unrelated product of Sanofi Genzyme. D.M.N. is a member of Sanofi Genzyme speakers’ bureau. A.M.-W., C.S., A.M.J., and S.R. are employees of Sanofi Genzyme. P.S.K. has received research support and honoraria from and holds Pompe and Gaucher Disease Registries’ advisory board membership at Sanofi Genzyme; has received grants and honoraria from Shire Pharmaceuticals, Valerion, Amicus; and Alexion Pharmaceuticals, Inc., and holds advisory board membership at Baebies, Inc. The other authors declare no conflicts of interest.