Reid Thompson, W.
Hornby, Brittany
Manuel, Ryan
Bradley, Elena
Laux, Janice
Carr, Jim
Vernon, Hilary J. http://orcid.org/0000-0001-9940-9866
This article is maintained by: Elsevier
Article Title: A phase 2/3 randomized clinical trial followed by an open-label extension to evaluate the effectiveness of elamipretide in Barth syndrome, a genetic disorder of mitochondrial cardiolipin metabolism
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/s41436-020-01006-8
Content Type: article
Copyright: © 2021, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics