Li, Cindy
Desai, Ankit K.
Gupta, Punita
Dempsey, Katherine
Bhambhani, Vikas
Hopkin, Robert J.
Ficicioglu, Can
Tanpaiboon, Pranoot
Craigen, William J.
Rosenberg, Amy S.
Kishnani, Priya S. http://orcid.org/0000-0001-8251-909X
This article is maintained by: Elsevier
Article Title: Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/s41436-020-01080-y
Content Type: article
Copyright: © 2021, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics