Updates are available Erratum dated 2022-10-01
Click to view Erratum: https://doi.org/10.1016/j.gim.2022.08.011
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Authors
Diaz, George A.
Jones, Simon A.
Scarpa, Maurizio
Mengel, Karl Eugen
Giugliani, Roberto
Guffon, Nathalie
Batsu, Isabela
Fraser, Patricia A.
Li, Jing
Zhang, Qi
Ortemann-Renon, Catherine
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More Information
This article is maintained by: Elsevier
Article Title: One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/s41436-021-01156-3
Content Type: article
Copyright: © 2021, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics
