Carrillo, Nuria http://orcid.org/0000-0003-0374-0808
Malicdan, May C.
Leoyklang, Petcharat
Shrader, Joseph A.
Joe, Galen
Slota, Christina
Perreault, John
Heiss, John D.
Class, Bradley
Liu, Chia-Ying
Bradley, Kennan
Jodarski, Colleen
Ciccone, Carla
Driscoll, Claire
Parks, Rebecca
Van Wart, Scott
Bayman, Levent
Coffey, Christopher S.
Quintana, Melanie
Berry, Scott M.
Huizing, Marjan
Gahl, William A.
This article is maintained by: Elsevier
Article Title: Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study
Journal Title: Genetics in Medicine
CrossRef DOI link to publisher maintained version: https://doi.org/10.1038/s41436-021-01259-x
Content Type: article
Copyright: © 2021, The Author(s), under exclusive licence to the American College of Medical Genetics and Genomics