Platt, Frances M.
d’Azzo, Alessandra
Davidson, Beverly L.
Neufeld, Elizabeth F.
Tifft, Cynthia J.
Article History
First Online: 1 October 2018
Change Date: 17 May 2019
Change Type: Correction
Change Details: In the originally published version of Figure 3, APP was incorrectly linked to CMA. In addition, the label for NCP2 was omitted, and GlcSph was incorrectly labelled as GlcCer. This figure has now been corrected.
Change Date: 18 October 2018
Change Type: Correction
Change Details: In the version of the article originally published, in Figure 2 and the accompanying legend, LIMP 2 was incorrectly referred to as LIMP 1. The article has now been corrected.
Competing interests
: F.M.P. is a trustee of Gordon Research Conferences, Chair of the Scientific Advisory Board of the National Tay-Sachs & Allied Diseases Association (NTSAD), a cofounder of and consultant to IntraBio and a consultant to Actelion and Orphazyme. A.d.A. has received research support from Ultragenyx Pharmaceutical. B.L.D. founded Talee Bio, Inc. and Spark Therapeutics and is on the Scientific Advisory Board of Homology Medicines, Intellia Therapeutics, Prevail Therapeutics, Inc and Sarepta Therapeutics. E.F.N. has previously received funding from BioMarin and is a member of the Scientific Advisory Board of the National MPS Society. C.J.T. is supported by the Division of Intramural Research of the National Human Genome Research Institute of the NIH, US Department of Health and Human Services and is a member of the Scientific Advisory Board of NTSAD.