Mercuri, Eugenio
Sumner, Charlotte J.
Muntoni, Francesco http://orcid.org/0000-0002-9102-5232
Darras, Basil T.
Finkel, Richard S. http://orcid.org/0000-0002-9351-7054
Article History
Accepted: 23 June 2022
First Online: 4 August 2022
Competing interests
: E.M., C.J.S., F.M., B.T.D. and R.S.F. are all principal investigators for clinical studies and consultants for Roche, Biogen, Novartis and Scholar Rock.