Mercuri, Eugenio
Pera, Maria Carmela http://orcid.org/0000-0001-6777-1721
Scoto, Mariacristina
Finkel, Richard http://orcid.org/0000-0002-9351-7054
Muntoni, Francesco http://orcid.org/0000-0002-9102-5232
Article History
Accepted: 7 September 2020
First Online: 14 October 2020
Competing interests
: E.M. is involved as an investigator in clinical trials for AveXis, Biogen, Roche and Scholar Rock. He has received honoraria for participating in symposia and advisory boards for AveXis, Biogen, Roche and Scholar Rock. His institution receives funding from Biogen for the coordination of an Italian registry for SMA, iSMAC. M.C.P. is involved as an investigator in clinical trials for AveXis, Biogen, Roche and Scholar Rock. She has received honoraria for participating in symposia and advisory boards for Biogen and Roche. Her institution receives funding from Biogen for the coordination of an Italian registry for SMA, iSMAC. M.S. is involved as an investigator in clinical trials for AveXis, Biogen and Roche. She has received honoraria for participating in symposia and advisory boards for AveXis, Biogen and Roche. Her institution receives funding from Biogen for the coordination of a UK-wide registry for SMA, SMA REACH UK. R.F. is involved as an investigator in clinical trials for AveXis, Biogen, Cytokinetics, Ionis, Roche and Scholar Rock. He has received honoraria for participating in symposia and advisory boards for AveXis, Biogen, Cytokinetics, Ionis, Roche and Scholar Rock. His institution receives funding from Biogen for the coordination of a US registry for SMA, iSMAC. F.M. is involved as an investigator in clinical trials for AveXis, Biogen and Roche. He has received honoraria for participating in symposia and advisory boards for AveXis, Biogen and Roche. His institution receives funding from Biogen for the coordination of a UK-wide registry for SMA, SMA REACH UK.