Wolf, Nicole I. http://orcid.org/0000-0003-1721-0728
ffrench-Constant, Charles
van der Knaap, Marjo S.
Article History
Accepted: 2 November 2020
First Online: 15 December 2020
Competing interests
: N.I.W. is a member of advisory boards for Ionis, Passage Bio and Takeda Shire.