Boulad, Farid
Maggio, Aurelio
Wang, Xiuyan
Moi, Paolo
Acuto, Santina
Kogel, Friederike http://orcid.org/0000-0002-8888-2268
Takpradit, Chayamon
Prockop, Susan
Mansilla-Soto, Jorge
Cabriolu, Annalisa http://orcid.org/0000-0002-8216-2120
Odak, Ashlesha http://orcid.org/0000-0001-5595-0394
Qu, Jinrong
Thummar, Keyur
Du, Fang
Shen, Lingbo
Raso, Simona
Barone, Rita
Di Maggio, Rosario
Pitrolo, Lorella
Giambona, Antonino
Mingoia, Maura
Everett, John K.
Hokama, Pascha
Roche, Aoife M.
Cantu, Vito Adrian http://orcid.org/0000-0002-3168-5140
Adhikari, Hriju http://orcid.org/0000-0001-9959-298X
Reddy, Shantan
Bouhassira, Eric
Mohandas, Narla
Bushman, Frederic D.
Rivière, Isabelle
Sadelain, Michel http://orcid.org/0000-0002-9031-8025
Funding for this research was provided by:
Stavros Niarchos Foundation
Cooley’s Anemia Foundation
Leonardo Giambrone Foundation Errant Gene Therapy
Memorial Hospital Research fund
Article History
Received: 28 February 2021
Accepted: 23 September 2021
First Online: 3 January 2022
Competing interests
: The authors declare no competing interests. The TNS9.3.55 vector technology has been granted to Errant Gene Therapy without financial compensation.