Habib, Al-Rahim R.
Kajbafzadeh, Majid
Desai, Sameer
Yang, Connie L.
Skolnik, Kate
Quon, Bradley S.
Article History
Received: 25 June 2018
Accepted: 27 April 2019
First Online: 10 May 2019
Competing Interests
: B.S.Q. has received consulting fees from Proteostasis Therapeutics Inc. and Horizon Pharma and has served as site PI for Vertex sponsored clinical trials.