Article History
Received: 10 July 2019
Accepted: 7 April 2020
First Online: 29 April 2020
Competing interests
: J. Vissing has received research and travel support, speaker honoraria from and/or served as consultant on advisory boards for Sanofi/Genzyme, Ultragenyx Pharmaceuticals, and Santhera Pharmaceuticals, Sarepta Therapeutics, Audentes Therapeutics, and Stealth Biotherapeutics. J. Dahlqvist reports no disclosures. R. Salim reports no disclosures. C. Thomsen reports no disclosures.