Egeland, Martin T.
Tarczyluk-Wells, Marta M.
Asmar, Melissa M.
Adintori, Evan G.
Lawrence, Roger
Snella, Elizabeth M.
Jens, Jackie K.
Crawford, Brett E.
Wait, Jill C. M.
McCullagh, Emma
Pinkstaff, Jason
Cooper, Jonathan D.
Ellinwood, N. Matthew
Funding for this research was provided by:
BioMarin Pharmaceutical
Allievex
Article History
Received: 15 January 2020
Accepted: 13 October 2020
First Online: 23 November 2020
Competing interests
: RL, BEC, and JCMW are employees and stockholders of BioMarin Pharmaceutical Inc. EGA, EM and JP were employees of BioMarin Pharmaceutical Inc. at the time of the study. MTE, MTW, EMS, JKJ and NME have received research support from BioMarin Pharmaceutical Inc. JC also had research support from BioMarin Pharmaceutical Inc. in addition to Abeona Therapeutics Inc., Regenexbio Inc. and CereSpir Inc. MMA has no competing interests to declare.