Taghizadeh, Leyla A.
King, Carina J.
Nascene, David R.
Gupta, Ashish O.
Orchard, Paul J.
Higgins, LeeAnn
Markowski, Todd W.
Nolan, Erin E.
Furcich, Justin W.
Lund, Troy C.
Article History
Received: 16 December 2021
Accepted: 19 April 2022
First Online: 14 May 2022
Competing interests
: P.J.O, T.C.L., D.R.N. are investigators for bluebird bio, Inc’s sponsored gene therapy study for cALD (Starbeam). L.A.T., C.J.K., A.O.G., L.H., T.W.M., E.E.N., and J.W.F. declare no competing interests.