Marulanda, Juliana
Tauer, Josephine T.
Boraschi-Diaz, Iris
Bardai, Ghalib
Rauch, Frank
Article History
Received: 18 November 2022
Accepted: 24 March 2023
First Online: 27 March 2023
Competing interests
: Frank Rauch: Ultragenyx Inc: Study grant to institution. Catabasis: Study grant to institution. Ibsen: Advisory Board. Sanofi: Advisory Board. The other authors declare no competing interests.