Jalnapurkar, Isha https://orcid.org/0000-0003-2437-9898
Frazier, Jean A.
Roth, Mark
Cochran, David M.
Foley, Ann
Merk, Taylor
Venuti, Lauren
Ronco, Lucienne
Raines, Shane
Cadavid, Diego
Funding for this research was provided by:
Fulcrum Therapeutics
Article History
Received: 30 November 2021
Accepted: 26 October 2022
First Online: 9 December 2022
Declarations
:
: This study was approved by the Institutional Review Board of the University of Massachusetts Chan Medical School (no. H00013963). Written informed consent was obtained from a parent or legal guardian prior to the study.
: N/A
: L. R., M. R., and D. C. were full-time employees of the Fulcrum Therapeutics during the experimental work and writing of the manuscript. They are no longer with Fulcrum Therapeutics, but they own equity in Fulcrum Therapeutics. D. C. and M. R. are currently full-time employees of X4 Pharmaceuticals, which is not related to this work. J. A. F. receives research support from Healx, Tetra, and Quadrant. D. M. C. consults with Abbvie Inc. The other authors declare that they have no competing interests.