Landi, Annalisa
Mimouni, Yanis
Demoisy, Anne
Namorado, Joana
Torretta, Silvia
D’Ercole, Annunziata
Alamo, Marta Del
Gibson, Spencer
Julkowska, Daria
Giannuzzi, Viviana
Funding for this research was provided by:
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Joint Programme on Rare Diseases (825575)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
European Rare Diseases Research Alliance (101156595)
Article History
Received: 10 June 2025
Accepted: 19 December 2025
First Online: 17 March 2026
Declarations
:
: Not applicable.
: Not applicable.
: The authors declare no competing interests.