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Gene therapy for ultrarare diseases: a geneticist’s perspective

Crossref DOI link: https://doi.org/10.1186/s12929-024-01070-1

Published Online: 2024-08-13

Update policy: https://doi.org/10.1007/springer_crossmark_policy

Authors

Hwu, Wuh-Liang https://orcid.org/0000-0001-6690-4879
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Text and Data Mining valid from 2024-08-13

Version of Record valid from 2024-08-13
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Article History

Received: 4 May 2024

Accepted: 6 August 2024

First Online: 13 August 2024

Declarations

:

: Not applicable.

: Not applicable.

: WLH received honoraria and royalty from PTC Therapeutics.