Ferri Grazzi, Enrico
Hawes, Charles
Camp, Charlotte
Hinds, David
O’Hara, Jamie
Burke, Tom
Article History
Received: 27 April 2023
Accepted: 24 June 2024
First Online: 29 July 2024
Declarations
:
: The CHESS II study received ethics approval from the University of Chester Ethics Committee. All patients or their legal representatives provided signed informed consent to participate in this study.
: Not applicable.
: EFG, JOH and TB are employees of HCD Economics Ltd., a consultancy which received research funding from BioMarin Europe for this study; CC, CH and DH are employees and stockholders of BioMarin Pharmaceutical, Inc.