Pressure for drug development in lysosomal storage disorders – a quantitative analysis thirty years beyond the US orphan drug act
Crossref DOI link: https://doi.org/10.1186/s13023-015-0262-5
Published Online: 2015-04-18
Published Print: 2015-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Mechler, Konstantin
Mountford, William K
Hoffmann, Georg F
Ries, Markus https://orcid.org/0000-0002-5054-5741
License valid from 2015-04-18
Article History
Received: 2 March 2015
Accepted: 6 April 2015
First Online: 18 April 2015