Immunogenicity of idursulfase and clinical outcomes in very young patients (16 months to 7.5 years) with mucopolysaccharidosis II (Hunter syndrome)
Crossref DOI link: https://doi.org/10.1186/s13023-015-0265-2
Published Online: 2015-04-24
Published Print: 2015-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Pano, Arian
Barbier, Ann J
Bielefeld, Bonnie
Whiteman, David AH
Amato, David A
License valid from 2015-04-24