Stable or improved neurological manifestations during miglustat therapy in patients from the international disease registry for Niemann-Pick disease type C: an observational cohort study
Crossref DOI link: https://doi.org/10.1186/s13023-015-0284-z
Published Online: 2015-05-28
Published Print: 2015-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
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Patterson, Marc C https://orcid.org/0000-0002-1116-126X
Mengel, Eugen
Vanier, Marie T
Schwierin, Barbara
Muller, Audrey
Cornelisse, Peter
Pineda, Mercè
License valid from 2015-05-28