Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study
Crossref DOI link: https://doi.org/10.1186/s13023-015-0326-6
Published Online: 2015-09-04
Published Print: 2015-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Suhr, Ole B
Coelho, Teresa
Buades, Juan
Pouget, Jean
Conceicao, Isabel
Berk, John
Schmidt, Hartmut
Waddington-Cruz, Márcia
Campistol, Josep M.
Bettencourt, Brian R.
Vaishnaw, Akshay
Gollob, Jared
Adams, David