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Recommendations on clinical trial design for treatment of Mucopolysaccharidosis Type III

Crossref DOI link: https://doi.org/10.1186/s13023-017-0675-4

Published Online: 2017-06-26

Published Print: 2017-12

Update policy: https://doi.org/10.1007/springer_crossmark_policy

Authors

Ghosh, Arunabha

Shapiro, Elsa

Rust, Stewart

Delaney, Kathleen

Parker, Samantha

Shaywitz, Adam J

Morte, Adelaida

Bubb, Gillian

Cleary, Maureen

Bo, Tien

Lavery, Christine

Bigger, Brian W

Jones, Simon A