Mortality in patients with Sanfilippo syndrome
Crossref DOI link: https://doi.org/10.1186/s13023-017-0717-y
Published Online: 2017-10-23
Published Print: 2017-12
Update policy: https://doi.org/10.1007/springer_crossmark_policy
Lavery, Christine
Hendriksz, Chris J.
Jones, Simon A.
Funding for this research was provided by:
BioMarin Europe Ltd (1842)