,
Geberhiwot, Tarekegn https://orcid.org/0000-0002-3629-2338
Moro, Alessandro
Dardis, Andrea
Ramaswami, Uma
Sirrs, Sandra
Marfa, Mercedes Pineda
Vanier, Marie T.
Walterfang, Mark
Bolton, Shaun
Dawson, Charlotte
Héron, Bénédicte
Stampfer, Miriam
Imrie, Jackie
Hendriksz, Christian
Gissen, Paul
Crushell, Ellen
Coll, Maria J.
Nadjar, Yann
Klünemann, Hans
Mengel, Eugen
Hrebicek, Martin
Jones, Simon A.
Ory, Daniel
Bembi, Bruno
Patterson, Marc
Funding for this research was provided by:
Consumers, Health, Agriculture and Food Executive Agency (2012 12 01)
Article History
Received: 24 November 2017
Accepted: 13 March 2018
First Online: 6 April 2018
Ethics approval and consent to participate
: Not applicable.
: Not applicable.
: AD, BB,TH, YN, SJ, MW, DO, SS, PG, MS, UR, MTV and MP has received travel grant from Actelion. Shire has provided funding to YN, SJ, SS, MTV, AD, BB, MH and MP. Genzyme has provided funding to YN, SJ, SS, JI, MH and MP. Orphazyme has provided funding to JI, AD and BB. Alexion has provided funding to SS and MP. Vtesse has provided travel grants to MTV and MP. SS has received funding from Biomarin and Pfizer. MP has received funding from Agio, Amicus and Novartis. SJ has received funding from Biomarin, Ultragenyx, PTC and Orchard Theraputics.
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