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Article History

Received: 27 July 2020

Accepted: 14 September 2020

First Online: 13 October 2020

Ethics approval and consent to participate

: The study design was approved by institutional IRB and study participants consented to participate. IRB institutional number: 0006-20-SZMC.

: Not applicable.

: The SZMC Gaucher Unit receives support from Sanofi/Genzyme for participation in the ICGG Registry, from Takeda for the GOS Registry, and Pfizer for TALIAS. The Unit also receives research grants from Takeda, Pfizer, Sanofi/Genzyme and Centogene. J.S. has received grant/research support and honoraria from Alexion, Amgen, Celgene, Merck Sharp & Dohme, Novartis, Pfizer, Prevail Therapeutics, Sanofi, and Takeda. A.Z. receives honoraria from Takeda and Pfizer and consultancy fee from Takeda, Prevail therapeutics and Bio-Events. S.R.-V. receives grant/research support, honoraria and advisory fee from Takeda, Pfizer, Sanofi/Genzyme and Prevail therapeutics.