Burgess, Nicholas M.
Kelso, Wendy
Malpas, Charles B.
Winton-Brown, Toby
Fazio, Timothy
Panetta, Julie
De Jong, Gerard
Neath, Joanna
Atherton, Sonny
Velakoulis, Dennis
Walterfang, Mark https://orcid.org/0000-0002-1389-3691
Funding for this research was provided by:
BioMarin Pharmaceutical
Article History
Received: 14 September 2020
Accepted: 22 December 2020
First Online: 18 January 2021
Ethics approval and consent to participate
: Research and ethics approval for the project was provided by the Melbourne Health Human Research Ethics Committee (MH Project Number 2014.113).
: All participants provided informed consent to participate in the trial.
: MW has received honoraria for conference presentations by Biomarin Pharmaceuticals.