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Authors
McGovern, Margaret M. http://orcid.org/0000-0002-7412-7536
Wasserstein, Melissa P.
Bembi, Bruno
Giugliani, Roberto
Mengel, K. Eugen
Vanier, Marie T.
Zhang, Qi
Peterschmitt, M. Judith
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Funding
Funding for this research was provided by:
Sanofi Genzyme
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Article History
Received: 1 December 2020
Accepted: 23 April 2021
First Online: 10 May 2021
Declarations
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: This study was approved prior to data collection by the Institutional Review Board, Ethics Committee, or Human Subjects Safety Committee at each site and voluntary, written informed consent was obtained from each patient and/or guardian. When appropriate, children also gave assent prior to any study procedures.
: All participants provided approval for publication of study data in an anonymized form.
: MMM has received honoraria and travel reimbursement from Sanofi Genzyme for participation in advisory boards. BB and MTV have received investigator fees from Sanofi Genzyme. MW, RG and EM have received investigator fees, honoraria, and reimbursement of travel expenses to attend scientific meetings from Sanofi Genzyme. QZ and MJP are employees of Sanofi Genzyme.
