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Authors
Genevaz, Delphine
Arnoux, Armelle
Marcel, Catherine
Brassier, Anaïs
Pichard, Samia
Feillet, François
Labarthe, François
Chabrol, Brigitte
Berger, Marc
Lapointe, Anne-Sophie
Frigout, Yvann
Héron, Bénédicte
Chatellier, Gilles
Belmatoug, Nadia https://orcid.org/0000-0002-7917-741X
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Funding
Funding for this research was provided by:
vaincre les maladies lysosomales
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Article History
Received: 2 July 2021
Accepted: 6 February 2022
First Online: 21 February 2022
Declarations
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: Informed consent was signed by all patients or parents. The study obtained all regulatory authorizations (opinion of the Advisory Committee on the Processing of Healthcare Information—CCTIRS) and a favorable rating from the ethics committee (CPP Île de France II # 2015-05-06). The research was conducted in the investigation centers in accordance with the Declaration of Helsinki and the Good Clinical Practices in force. Anonymized data was used for analysis and publication.
: Not applicable.
: The authors declared that they have no competing interests in relation to this study.
