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Article History

Received: 30 November 2021

Accepted: 20 February 2022

First Online: 4 March 2022

Declarations

:

: All patients with Pompe disease are included in an over-arching follow-up study, which previously has been approved of by the Medical Ethics Review Committee (Dutch: Medisch Ethische ToetsingsCommissie (METC)) of the Erasmus Medical Centre. SARS-CoV-2 infections have been classed as an Adverse Event (AE) in the longitudinal study and therefore, included patients fall under the aforementioned protocol. All procedures followed were in accordance with the ethical standards of the responsible committee on human experimentation (institutional and national) and with the Helsinki Declaration of 1975, as revised in 2000. Informed consent was obtained from all parents of patients for being included in the study.

: All patients included in this paper verbally approved to have their data anonymously presented in this article. If patients were < 16 years old, parents or legal guardians approved of publication. Patients between the ages of 16 and 18 both approved themselves and had their parents or legal guardians approve.

: ATvdP received funding for research, clinical trials, and advisory fees from Sanofi-Genzyme, Amicus Therapeutics, Biomarin, Ultragenix, Sarepta, Audentes, and Spark Therapeutics working on enzyme replacement therapy or next-generation therapies in the field of Pompe disease, other lysosomal storage diseases or neuromuscular disorders, under agreements with Erasmus MC University Medical Center and the relevant industry. JMPvdH received funding for research, clinical trials, and advisory fees from Sanofi-Genzyme, Amicus Therapeutics, Biomarin, Sarepta, and Chiesi working on enzyme replacement therapy or next-generation therapies in the field of Pompe disease, other lysosomal storage diseases or neuromuscular disorders, under agreements with Erasmus MC University Medical Center and the relevant industry.