Donald, Aimee https://orcid.org/0000-0002-2623-5233
Björkvall, Cecilia Kämpe
Vellodi, Ashok
,
Cox, Timothy M.
Hughes, Derralyn
Jones, Simon A.
Wynn, Robert
Machaczka, Maciej
Funding for this research was provided by:
Medical Research Council
National Institute for Health Research (IS-BRC-1215-20014)
Article History
Received: 12 January 2022
Accepted: 6 June 2022
First Online: 18 June 2022
Declarations
:
: Patients enrolled in the UK Gaucherite study who contributed data were consented using standard informed written and verbal consent procedures, the study underwent ethical review by the UK Ethics committee (Essex; REC ref 14/EE/1168) and Good Clinical Practice was observed throughout. Swedish patients contributed data under an equivalent process and the declaration of Helsinki underlines the principles of all the research data contained.
: Although individual patient data is included in the manuscript, none are identifiable and consent for publication of anonymised data included in the recruitment process/ethical review.
: The authors declare that they have no competing interests.