Document is current
Any future updates will be listed below
-
Authors
-
Funding
Funding for this research was provided by:
National Niemann-Pick Disease Foundation
- License Information
-
More Information
Article History
Received: 2 May 2022
Accepted: 15 August 2022
First Online: 2 September 2022
Declarations
:
: All study procedures were in accordance with ethical standards of the 1964 Helsinki Declaration and its later amendments, relevant laws, and institutional guidelines and approved by the Western Institutional Review Board and Copernicus Group Institutional Review Board. Online written informed consent was obtained from all participants or their caregivers.
: Online written consent for publication of aggregated and individual anonymized data was obtained from all respondents.
: GAD is an investigator on a clinical trial of olipudase alfa sponsored by Sanofi and served as a scientific consultant to Sanofi. JC and JH declare that they have no competing interests.
