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Article History

Received: 30 December 2022

Accepted: 4 June 2023

First Online: 4 August 2023

Declarations

: <b>Ethics approval and consent to participate</b>.

: Patients or their caregivers, as appropriate, gave their informed consent for nusinersen treatment (National Health System form for reimbursed treatment program) and for data collection (Ethic Committee approval- BK/180/2008).

: <b>Consent for publication</b>.

: Not applicable.

: AL and AK-P received honoraria for advisory boards and speaking at educational events for Biogen, Novartis/AveXis, PTC and Roche; AL is a subinvestigator for SUNFISH and JEWELFISH studies; AK-P is a Principal Investigator for SUNFISH and JEWELFISH studies; AK-P and AL are involved in project supported with Institutional grant to Medical University of Warsaw from Biogen POL-SMG-17-11166 (5BIOGEN01); AW, AF, KA-G, ZG-W and RN received honoraria for speaking at educational events for Biogen and Roche; AP-Ch received honoraria for speaking at educational events for Biogen and PTC and is a subinvestigator in the DMD study; MB, PB, GR, DK, KM declare no conflict of interest.

: The Department of Neurology at the Medical University of Warsaw, Poland, is a member of the European Reference Network for Rare Neuromuscular Diseases (EURO-NMD).