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Authors
Fortunato, Fernanda
Bianchi, Francesca
Ricci, Giulia
Torri, Francesca
Gualandi, Francesca
Neri, Marcella
Farnè, Marianna
Giannini, Fabio
Malandrini, Alessandro
Volpi, Nila
Lopergolo, Diego
Silani, Vincenzo
Ticozzi, Nicola
Verde, Federico
Pareyson, Davide
Fenu, Silvia
Bonanno, Silvia
Nigro, Vincenzo
Peduto, Cristina
D’Ambrosio, Paola
Zeuli, Roberta
Zanobio, Mariateresa
Picillo, Esther
Servidei, Serenella
Primiano, Guido
Sancricca, Cristina
Sciacco, Monica
Brusa, Roberta
Filosto, Massimiliano
Cotti Piccinelli, Stefano
Pegoraro, Elena
Mongini, Tiziana
Solero, Luca
Gadaleta, Giulio
Brusa, Chiara
Minetti, Carlo
Bruno, Claudio
Panicucci, Chiara
Sansone, Valeria A.
Lunetta, Christian
Zanolini, Alice
Toscano, Antonio
Pugliese, Alessia
Nicocia, Giulia
Bertini, Enrico
Catteruccia, Michela
Diodato, Daria
Atalaia, Antonio
Evangelista, Teresinha
Siciliano, Gabriele
Ferlini, Alessandra https://orcid.org/0000-0001-8385-9870
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Funding
Funding for this research was provided by:
Sarepta Therapeutics (r4567)
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Article History
Received: 15 September 2022
Accepted: 18 June 2023
First Online: 21 July 2023
Declarations
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: All patients have signed a specific consent to have data uploaded in CPMS platform, to have data available for databases and registries and to have data available for researches. This consent process was established by DG SANTE in collaboration with the legal and ethical working group of the ERNs. A common, information and consent form, complying with GDPR, was translated in 24 EU languages and is available to be used across all ERNs.
: Not applicable.
: Not applicable.
