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Authors
Yee, Karen S.
Chirila, Costel
Davenport, Eric
Mladsi, Deirdre
Barnett, Christine
Kronenberger, William G. https://orcid.org/0000-0001-8543-9941
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Clinical Trials BETA
Clinical trials referenced in this document:
nct02055118 at ClinicalTrials.govnct02412787 at ClinicalTrials.govDocuments that mention this clinical trial
A post hoc analysis of Projected Retained Ability Scores (PRAS) for the longitudinal assessment of cognitive functioning in patients with neuronopathic mucopolysaccharidosis II receiving intrathecal idursulfase-IT
https://doi.org/10.1186/s13023-023-02957-2
Documents that mention this clinical trial
A post hoc analysis of Projected Retained Ability Scores (PRAS) for the longitudinal assessment of cognitive functioning in patients with neuronopathic mucopolysaccharidosis II receiving intrathecal idursulfase-IT
https://doi.org/10.1186/s13023-023-02957-2
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Funding
Funding for this research was provided by:
Takeda Development Center Americas, Inc.
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Article History
Received: 7 June 2023
Accepted: 20 October 2023
First Online: 2 November 2023
Declarations
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: The phase 2/3 trial and its extension were approved by the relevant institutional review boards/independent ethics committees and conducted in accordance with the Declaration of Helsinki and International Conference on Harmonization Good Clinical Practice guidelines. Written informed consent was obtained from parents or legal guardians.
: Not applicable.
: KSY was an employee of Takeda Development Center Americas, Inc. and stockholder of Takeda Pharmaceuticals Company Limited at the time of the analysis (current affiliation is Alexion Pharmaceuticals, Inc., AstraZeneca Rare Disease, Boston, MA, USA). CC, ED, DM, and CB are employees of RTI Health Solutions, and conducted contracted research for Takeda Pharmaceuticals Company Limited. WGK has received consulting fees from Homology Medicines, Indiana Hemophilia and Thrombosis Center, and Takeda Pharmaceuticals Company Limited.
