Al Yaarubi, Saif http://orcid.org/0000-0003-0228-1304
Alsagheir, Afaf
Al Shidhani, Azza
Alzelaye, Somaya
Alghazir, Nadia
Brema, Imad
Alsaffar, Hussain
Al Dubayee, Mohammed
Alshahrani, Awad
Abdelmeguid, Yasmine
Omar, Omneya M.
Attia, Najya
Al Amiri, Elham
Al Jubeh, Jamal
Algethami, Albandari
Alkhayyat, Haya
Haleem, Azad
Al Yahyaei, Mouza
Khochtali, Ines
Babli, Saleha
Nugud, Ahmed
Thalange, Nandu
Albalushi, Sarah
Hergli, Nadia
Deeb, Asma
Alfadhel, Majid
Funding for this research was provided by:
Amryt Pharmaceuticals
Article History
Received: 6 April 2023
Accepted: 13 February 2024
First Online: 13 March 2024
Declarations
:
: Approval for participation in this retrospective research was obtained from the ethics committee or institutional review board at participating medical centers. The Declaration of Helsinki and Guideline for Good Clinical Practice from the International Conference on Harmonization were adhered to throughout this project [CitationRef removed, CitationRef removed]. As per local regulations, written consent was not necessary for the use of retrospective anonymized (unidentifiable) data; however, all subjects (or their legal guardians) provided written consent for genetic testing.
: This retrospective analysis only reports summary data and no individual patient details are reported.
: None of the authors has any conflicting interests to disclose.