Schulz, Angela
Patel, Nita http://orcid.org/0009-0008-5377-6482
Brudvig, Jon J.
Stehr, Frank
Weimer, Jill M.
Augustine, Erika F.
Funding for this research was provided by:
Amicus Therapeutics (N/A)
Article History
Received: 28 November 2023
Accepted: 3 March 2024
First Online: 18 March 2024
Declarations
:
: The methods used in this study were approved by the Western Institutional Review Board (IRB Tracking Number 20210943). All participants provided written informed consent prior to participating in the study.
: Not applicable.
: N.P., J.J.B., and J.M.W. are employees of Amicus Therapeutics, a company that develops therapies for rare diseases including CLN3 disease.