Souza, Paulo Victor Sgobbi
Haselkorn, Tmirah
Baima, Jader
Oliveira, Renato Watanabe
Hernández, Fabián
Birck, Marina G.
França, Marcondes C. Jr
Funding for this research was provided by:
Astellas Gene Therapies (Astellas Gene Therapies)
Article History
Received: 20 June 2023
Accepted: 24 March 2024
First Online: 7 May 2024
Declarations
:
: In accordance with Brazilian ethical resolution number 510, ethics committee approval was not required for this secondary study using anonymized data.
: This study contains anonymized patient data. No direct patient identifiers have been provided in this manuscript.
: Individual patient consent was not required for this secondary study using anonymized data from a public healthcare system database.
: PVSS is a neurologist, assistant at Ambulatório de Doenças Neuromusculares (UNIFESP-EPM); TH and JB are employees and shareholders of Astellas Gene Therapy. CP is a consultant to Astellas Gene Therapy. RWO, FH, and MGB are employees of IQVIA. MF is a professor at the School of Medicine at UNICAMP.