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Authors
Desguerre, Isabelle
Barrois, Rémi http://orcid.org/0000-0001-8877-5035
Audic, Frédérique
Barnerias, Christine
Chabrol, Brigitte
Davion, Jean Baptiste
Durigneux, Julien
Espil-Taris, Caroline
Gomez-Garcia de la Banda, Marta
Guichard, Marine
Isapof, Arnaud
Nougues, Marie Christine
Laugel, Vincent
Le Goff, Laure
Mercier, Sandra
Pervillé, Anne
Richelme, Christian
Thibaud, Marie
Sarret, Catherine
Schweitzer, Cyril
Testard, Hervé
Trommsdorff, Valérie
Vanhulle, Catherine
Walther-Louvier, Ulrike
Altuzarra, Cécilia
Chouchane, Mondher
Ropars, Juliette
Quijano-Roy, Susana
Cances, Claude
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Funding
Funding for this research was provided by:
Agence Nationale de Sécurité du Médicament et des Produits de Santé
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Article History
Received: 9 May 2023
Accepted: 18 August 2024
First Online: 13 September 2024
Declarations
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: All families provided informed written consent after thorough explanations of the study goals and procedures were given. The local ethics committee and the committee on human research, Est-III, granted authorization to perform this study (IRB approval statement; MR004: 2206723 v 0) in accordance with the Declaration of Helsinki.
: All the authors provided their consent for publication of the present version of the manuscript.
: SQR serves as a Scientific Advisory Board member for NOVARTIS GT, BIOGEN, and ROCHE and is the principal investigator in clinical trials for all three companies. MGGB is a subinvestigator in SMA studies and serves as a Scientific Advisory Board member for all three companies.
