Funding for this research was provided by:
Asociación Cistinosis España (Asociación Cistinosis España)
Article History
Received: 2 April 2024
Accepted: 13 October 2024
First Online: 5 November 2024
Declarations
:
: The Ethics Committee of the Vall d’Hebron University Hospital (Barcelona, Spain) approved the study. Informed consent was obtained from all participants.
: Not applicable.
: GA reports receiving consulting fees from Alexion, AstraZeneca Rare Disease, Chiesi, Advicenne, Recordati Rare Diseases, Dicerna, and Alnylam; and lecture fees from Alexion, AstraZeneca Rare Disease, Chiesi, Advicenne, Kyowa Kirin, and Recordati Rare Diseases. The other authors do not have competing interests.