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Authors
Polak, Yasmin https://orcid.org/0009-0008-4730-354X
van Dussen, Laura
Kemper, E. Marleen
Vaz, Frédéric M.
Klouwer, Femke C. C.
Engelen, Marc
Hollak, Carla E. M.
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Article History
Received: 8 May 2024
Accepted: 11 November 2024
First Online: 19 December 2024
Declarations
:
: Not applicable.
: Not applicable.
: EK: Board member of the Dutch Hospital Pharmacist Association for which no personal fees are received. The association has no involvement in the preparation of this manuscript or interest in the product or patients described. FV: Consulting for Scenic Biotech, board member of the European Metabolic Group (EMG), secretary of the SSIEM Education and Training Advisory Committee (ETAC), inventor of a patent for a screening method of cerebrotendinous xanthomatosis (PCT/EP2018/055236). CH: Received grants from Sanofi, Idorsia and Protalix to perform clinical studies in the field of lysosomal storage disorders, these clinical studies are outside the scope of this manuscript and CH received no personal fees. All other authors declare no conflict of interest.
