Giugliani, Roberto https://orcid.org/0000-0001-9655-3686
de Siqueira, Ana Cecília Menezes
Santos, Emerson Santana
Leão, Emília Katiane E. A.
Carvalho, Gerson da Silva
Santos, Mara Lúcia Schmitz Ferreira
Raskin, Salmo
Martins, Ana Maria
Funding for this research was provided by:
JCR Pharmaceuticals (JCR Pharmaceuticals)
Article History
Received: 8 May 2024
Accepted: 15 November 2024
First Online: 26 November 2024
Declarations
:
: Not applicable.
: Not applicable.
: RG declares research funding and/or speaker honoraria and/or consulting fees, received from Allievex, Amicus, Astellas, Avrobio, Azafaros, BioMarin, Chiesi, JCR, Novartis, Paradigm, Passage Bio, PTC, Regenxbio, Sanofi, Takeda, and Ultragenyx. The other authors declare that they have no competing interests.