Lenders, Malte
Nowak, Albina
Cybulla, Markus
Kaufeld, Jessica
Köhn, Anja Friederike
Muschol, Nicole Maria
Kurschat, Christine
Brand, Eva https://orcid.org/0009-0004-3243-5508
Funding for this research was provided by:
Universitätsklinikum Münster
Article History
Received: 7 August 2024
Accepted: 7 December 2024
First Online: 27 December 2024
Declarations
:
: All investigations were performed after approval by the respective ethics committees of the participating centers (project number: 2016-401-f-S; 2011-347-f).
: Written informed consent for molecular analysis and publication was obtained from patients.
: ML received speaker honoraria, travel funding and research grants from Amicus Therapeutics, Sanofi Genzyme, Chiesi, and Takeda. AN received speaker honoraria and research grants from Amicus, Takeda and Sanofi Genzyme. AFK received speaker honoraria and/or travel grants from Amicus Therapeutics, Biomarin, Orphazyme, Sanofi Genzyme and Takeda. NMM is a consultant for Amicus Therapeutics, Biomarin, Chiesi, JCR, Sanofi Genzyme, Takeda, and Orphazyme and received speakers honoraria and travel grants from Amicus Therapeutics, Biomarin, Chiesi, Sanofi Genzyme, and Takeda. JK received speaker honoraria and/or travel funding from Amicus Therapeutics, Sanofi Genzyme, Chiesi, Novartis and Takeda. CK received speaker honoraria and travel support from Amicus Therapeutics, Chiesi, Eleva, Sanofi Genzyme, and Takeda. MC received speaker honoraria/travel grants from Takeda, Amicus Therapeutics, Idorsia, and Alexion. EB received research grants and speaker honoraria from Sanofi Genzyme, Takeda, Chiesi, Eleva, and Amicus Therapeutics.