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Authors
Hwu, Wuh-Liang
Lee, Hui-Min
Peipert, John Devin
Zhang, Rongrong
Werner, Christian
Sierra, J. Rafael
O’Connell, Thomas
Woolley, Jonathan J.
Crowell, Marjorie
Wang, Antonia
Tomazos, Ioannis https://orcid.org/0000-0003-0290-4583
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Funding
Funding for this research was provided by:
PTC Therapeutics (PTC Therapeutics)
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Article History
Received: 22 July 2024
Accepted: 28 January 2025
First Online: 7 February 2025
Declarations
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: All three single-arm, open-label clinical trials were approved by the appropriate institutional and/or national research ethics committee and have been performed in accordance with the ethical standards as described in the Declaration of Helsinki. Written informed consent was obtained from trial participants or their parents in the case of children.
: Not applicable.
: RZ, JRS, AW, CW, and IT are/were employees of and may hold stocks in PTC Therapeutics at the time of writing. TO, JJW, and MC are employees of Medicus Economics, which received funding from PTC Therapeutics for this work. W-LH, H-ML, and JDP received consulting fees from PTC Therapeutics.
