Lenders, Malte
Nowak, Albina
Cybulla, Markus
Kaufeld, Jessica
Köhn, Anja Friederike
Muschol, Nicole Maria
Kurschat, Christine
Brand, Eva https://orcid.org/0009-0004-3243-5508
Funding for this research was provided by:
Universitätsklinikum Münster
Article History
Received: 9 December 2024
Accepted: 10 February 2025
First Online: 20 February 2025
Declarations
:
: All investigations were performed after approval by the respective ethics committees of the participating centers (project number: 2016-401-f-S; 2011-347-f).
: Written informed consent for molecular analysis and publication was obtained from patients.
: ML received speaker honoraria, travel funding and research grants from Amicus Therapeutics, Sanofi, Chiesi, Sumitomo Pharma, and Takeda. AN received speaker honoraria and research grants from Amicus, Takeda, and Sanofi. AFK received speaker honoraria and/or travel grants from Amicus Therapeutics, Biomarin, Orphazyme, Sanofi, and Takeda. NMM is a consultant for Amicus Therapeutics, Biomarin, Chiesi, JCR, Sanofi, Takeda, and Orphazyme and received speakers honoraria and travel grants from Amicus Therapeutics, Biomarin, Chiesi, Sanofi, and Takeda. JK received speaker honoraria and/or travel funding from Amicus Therapeutics, Sanofi, Chiesi, Novartis, and Takeda. CK received speaker honoraria and travel support from Amicus Therapeutics, Chiesi, Eleva, Sanofi, and Takeda. MC received speaker honoraria/travel grants from Takeda, Amicus Therapeutics, Idorsia, and Alexion. EB received research grants and speaker honoraria from Sanofi, Takeda, Chiesi, Eleva, and Amicus Therapeutics.