Kehrer, Christiane https://orcid.org/0000-0002-6313-1839
Bevot, Andrea
Martin, Pascal
Raabe, Christa
Gregor, Saskia
Krägeloh-Mann, Ingeborg
Groeschel, Samuel
Funding for this research was provided by:
Orchard Therapeutics
Universitätsklinikum Tübingen
Article History
Received: 8 July 2024
Accepted: 24 February 2025
First Online: 23 May 2025
Declarations
:
: The study (DRKS 00030287) was approved by the Ethical Committee of the University of Tübingen (Nr. 401/2005).
: All authors read and approved the final manuscript. Parents of the patients gave written consent for data acquisition, interviews by phone, as well as for publication of the study. Written consent forms are approved by the Ethical Committee of the University of Tübingen (Nr. 401/2005).
: The authors declare that they have no competing interests. The Orchard therapeutics team expressed no objections to the manuscript (26.06.2024).